Mini-COMET: Effects of Avalglucosidase Alfa on Ptosis in Participants With Infantile-Onset Pompe Disease Previously Treated With Alglucosidase Alfa
Author Type(s)
Faculty
Document Type
Abstract
Publication Date
4-2021
Journal Title
Molecular Genetics and Metabolism
Department
Pediatrics
Recommended Citation
Prakalapakorn, S. G., Davison, J., Broomfield, A., Kronn, D., Labarthe, F., Brassier, A., Hahn, S., Kumada, S., Ohki, H., Pichard, S., An Haack, K., Johnson, J., Meng, X., Chien, Y. H., Kishnani, P., & Mini-COMET Investigators. (2021). Mini-COMET: Effects of Avalglucosidase Alfa on Ptosis in Participants With Infantile-Onset Pompe Disease Previously Treated With Alglucosidase Alfa. Molecular Genetics and Metabolism, 132 (Suppl. 1), S137. https://doi.org/10.1016/S1096-7192(21)00296-1
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