Mini-COMET Study: Effects of Repeat Avalglucosidase Alfa Dosing on Ptosis in Participants With Infantile-Onset Pompe Disease (IOPD) Who Were Previously Treated With Alglucosidase Alfa
Author Type(s)
Faculty
Document Type
Abstract
Publication Date
2-2021
DOI
10.1016/j.ymgme.2020.12.058
Journal Title
Molecular Genetics and Metabolism
Department
Pediatrics
Recommended Citation
Davison, J., Brassier, A., Broomfield, A., Chien, Y., Hahn, S., Kronn, D., Kumada, S., Labarthe, F., Ohki, H., Pichard, S., Prakalapakorn, S. G., An Haack, K., Johnson, J., Meng, X., Kishnani, P. S., & MIni-COMET Investigators. (2021). Mini-COMET Study: Effects of Repeat Avalglucosidase Alfa Dosing on Ptosis in Participants With Infantile-Onset Pompe Disease (IOPD) Who Were Previously Treated With Alglucosidase Alfa. Molecular Genetics and Metabolism, 132 (2), S31-S32. https://doi.org/10.1016/j.ymgme.2020.12.058
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