NYMC Faculty Publications

Inflammatory Modulation by Cord Blood Stem Cells Prevented Digit Deformation in Recessive Dystrophic Epidermolysis Bullosa

Author Type(s)

Student, Faculty

DOI

10.1016/j.ymthe.2025.08.038

Journal Title

Molecular Therapy

First Page

5427

Last Page

5441

Document Type

Article

Publication Date

11-5-2025

Department

Pediatrics

Keywords

IL-1, immunomodulation, inflammation, LIF, RDEB, unrestricted somatic stem cells

Disciplines

Medicine and Health Sciences

Abstract

Unrestricted somatic stem cells (USSCs) ameliorated fibrosis, enhanced motility, and improved survival in an RDEB mouse model by modulating IL-1-driven inflammation and promoting wound-healing macrophages. LIF secretion from USSCs suppressed IL-1α and increased IL-1Ra in macrophages, highlighting the therapeutic potential of stem cell-mediated paracrine signaling in RDEB.

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