Mini-COMET Study: Individual Participant-Level Responses to Treatment in Patients With Infantile-Onset Pompe Disease Receiving Repeated Dose Regimens of Avalglucosidase Alfa or Alglucosidase Alfa Who Were Previously Treated With Alglucosidase Alfa
Author Type(s)
Faculty
Document Type
Abstract
Publication Date
2-2021
DOI
10.1016/j.ymgme.2020.12.128
Journal Title
Molecular Genetics and Metabolism
Department
Pediatrics
Recommended Citation
Kishnani, P. S., Brassier, A., Broomfield, A., Davison, J., Hahn, S., Kumada, S., Labarthe, F., Ohki, H., Pichard, S., An Haack, K., Johnson, J., Meng, X., Chien, Y., & Kronn, D. (2021). Mini-COMET Study: Individual Participant-Level Responses to Treatment in Patients With Infantile-Onset Pompe Disease Receiving Repeated Dose Regimens of Avalglucosidase Alfa or Alglucosidase Alfa Who Were Previously Treated With Alglucosidase Alfa. Molecular Genetics and Metabolism, 132 (2 Suppl.), S57-S58. https://doi.org/10.1016/j.ymgme.2020.12.128
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