Mini-COMET: Individual-Level Treatment Responses in Infantile-Onset Pompe Disease Participants Receiving Avalglucosidase Alfa or Alglucosidase Alfa Who Previously Received Alglucosidase Alfa

Author Type(s)

Faculty

Document Type

Abstract

Publication Date

4-2021

Journal Title

Molecular Genetics and Metabolism

Department

Pediatrics

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